Protein replacement therapy

Protein replacement therapy is a medical treatment that supplements or replaces a protein in patients in whom that particular protein is deficient or absent. There have been significant advances in this treatment. PRT is being tested in clinical trials with the diseases Progeria and Epidermolysis bullosa dystrophica as a potential treatment. For patients with Epidermolysis bullosa dystrophica there has been promising results.

See also

• Enzyme replacement therapy
• Gene therapy

Further reading

• Stegmann TJ (December 2006). "Protein Therapy vs. Gene Therapy". DDNEWS.